Projects per year
Search results
-
Active
Combining CRISPRa-mediated inhibition of fibrosis with U7snRNAmediated exon skipping for Dystrophin rescue for Duchenne muscular dystrophy gene therapy
March, J. (PI) & Malerba, A. (Mentor)
1/01/25 → 31/12/25
Project: Research
-
Improving protein folding to enhance microdystrophin expression in Duchenne muscular dystrophy
Malerba, A. (PI)
1/11/24 → 31/10/26
Project: Research
-
Protein folding strategies to enhance microdystrophin expression in Duchenne Muscular Dystrophy
Boulinguiez, A. (Fellow) & Malerba, A. (Mentor)
1/11/24 → 31/10/26
Project: Research
-
Replacing valproate with a safer, broad-spectrum drug for epilepsy treatment
Williams, R. (PI)
1/04/24 → 31/03/26
Project: Research